ASH Clinical News August 2017 v3 | Page 37

FEATURE Features The Geography of Drug Approvals How can regulators look at the same data and get different results? ASHClinicalNews.org The goal of regulatory bodies such as the U.S. Food and Drug Administration (FDA), the European Medicines Agency (EMA), and the African Medi- cines Agency is always the same: Balance potential benefits and risks to ensure that the drugs that make it to market are both safe and effective for patients in need. Still, a drug that gains FDA approval may give pause to European reviewers, despite having reviewed the same evidence as their American coun- terparts, and vice versa. These contrasting conclusions are, in part, due to each agency’s basic structure and processes: Both the FDA and the EMA have distinct interactions with external stakeholders, different methods of endpoint evaluation, and individual comfort levels with risk. ASH Clinical News spoke with representatives from each agency, as well as independent investiga- tors, to learn how the agencies make their decisions. The Road to Approval The road to approval is well-trodden: Once an advanced phase trial (or even an earlier phase study, through accelerated approval mechanisms) is completed and shows encouraging results, the company attempts to secure approval from the relevant regulatory bodies for the drug to enter the market. In the U.S., that means submitting a new drug application to the FDA’s Center for Drug Evaluation and Research – one of the FDA’s largest centers. The agency then has 60 days to decide whether the appli- cation should be filed for review. 1 Filed applications are then reviewed by a team of physicians , statisti- cians, chemists, and pharmacologists, who assess the data to determine the drug’s safety and efficacy for the proposed indication. Though FDA review is a strict, arduous process, ASH Clinical News 35